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Researchers use our
technologies in their quest
to cure diseases like cancer,
HIV, and Parkinson’s
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Gene Editing & Cell Reprogramming
mRNA Vectorization of Gene-Editing Proteins
Chromatin Context-Sensitive Gene-Editing Endonuclease
mRNA Cell Reprogramming
Combined mRNA Gene-Editing & Cell Reprogramming
Disease-Focused Technologies
Gene Editing Checkpoint Molecule Genes for the Treatment of Cancer
Gene-Editing Therapies for Alpha-1-Antitrypsin Deficiency
Gene-Editing Therapies for Epidermolysis Bullosa (EB)
mRNA Therapies for Dystrophic Epidermolysis Bullosa (DEB)
Gene-Editing Therapies for HIV
Gene-Editing Therapies for Parkinson’s Disease
Gene-Editing Therapies for Chronic Pain
Gene-Editing Therapies for Duchenne Muscular Dystrophy (DMD)
Nucleic-Acid Delivery
ToRNAdo™ Nucleic-Acid Delivery System
Insertion of Sequences into Safe-Harbor Loci
mRNA Delivery to Skin
Nucleic-Acid Delivery
We develop technologies for delivering nucleic acids to cells in vitro and in vivo.
Download our Technology Catalog
ToRNAdo™ Nucleic-Acid Delivery System
Insertion of Sequences into Safe-Harbor Loci
mRNA Delivery to Skin
Our technologies are protected by 90 patents in 14 countries
Review our patent library